Classification

9/14/2015 Types of Research Studies New Directions in MDS Treatment: What’s on the Horizon? Preclinical Clinical In vitro Observational In vivo ...
Author: Spencer Flynn
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9/14/2015

Types of Research Studies New Directions in MDS Treatment: What’s on the Horizon?

Preclinical

Clinical

In vitro

Observational

In vivo

Interventional (purpose) • Phase 1 (safe?)

Tim Graubert, MD

• Phase 2 (effective?)

Aplastic Anemia & MDS International Foundation Patient and Family Conference

• Phase 3 (superior?)

September 19, 2015

• Phase 4 (safety)

MDS: Diagnosis/Classification

MDS: Diagnosis/Classification

Cytopenia(s): • Hb